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AC-1202 is a first-in-class therapeutic that targets neuronal cells in the brain and acts to increase mitochondrial activity. Numerous studies have shown that energy metabolism and lipid homeostasis are impaired in neuronal cells within the hippocampal region of the brain where memory and cognition are processed. Research has shown that AC-1202 lowers oxidative stress in the brain while increasing energy metabolism essential for the synthesis of key neurotransmitters and lipids. Preclinical studies of AC-1202 have shown it to be effective in behavioral studies of learning and memory, and a Phase IIa clinical trial demonstrated that it improved certain measures of memory in Alzheimer's disease patients.
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